Grandparents Use DNA Analysis to Prevent and Treat Inherited Diseases for Future Generations

Why is DNA Analysis important to me?demonstrated that some of these polymorphisms are
Knowing your family's genetic history may somedayin genes whose functions are important in responses
save your life or that of someone you love. Basedof individual patient to therapy. The pathologist will
on state-of-the-art genetic technology, a unique DNAneed to profile common polymorphisms in patients
Profile can be generated for you to keep for yearswho are beginning therapy for common diseases
to come. DNA Storage for up to 25 years is availablesuch as diabetes, hypertension, cancer and infections.
for future genetic testing, upon your request. WhatThe laboratory definition of the genotype/phenotype
better gift can a loved one leave behind?will determine the specific drug and doses suitable for
What role does DNA have in Funeral Service?him. This puts the pathologist in a more definitive
The purpose of this article is to familiarize Funeralposition to determine appropriate therapy than
Directors about DNA activities, and related areas.traditional predictions of disease behavior based on
Realizing that this technology is what we asmorphology of lesions (microscopic patterns) or
caregivers are used to discussing, is a field that is ofcultural characteristics of infectious organisms. The lab
concern to many of our clients and their families. Thealso monitors the success of gene therapy. After a
vast spectrum of DNA can give us insight on thegene is introduced, the tissue where the gene is
value it can play in our community. In a series ofinserted (i.e.: Transgenic Monkey or Mouse) must be
articles, we would like to give you a basic knowledgeactive and should be monitored for normal expression
about the different but related studies involving DNA.of the introduced gene and normal structure and
It takes three generations to determinefunction of the gene product. The lab must also
predisposition to most of the genetic inheritedmonitor the "integrating transfected genes" such that
diseases / disorders. It is now known that familiesintegration allows both normal gene expression and
should store DNA for future use. Banking specimensdoes not produce abnormal function or structure of
containing DNA from the same Family providesthe patient's other genes. In summary, molecular
invaluable information for the health of current andpathology is permeating and penetrating, as was
future offspring. We as Funeral Directors have animmunopathology 20 years ago. "Immunopathology"
opportunity to make a Family aware that such aan example of which is vaccine therapy is nothing
service is available. After burial, retrieving DNA can benew, a German/Austrian vaccine "UKRAIN" is
expensive. Obtaining DNA after cremation is muchsupposed to destroy cancer cells through
more difficult. The success rate of recovering DNAAPOPTOSOS (programmed cell death) without
within the first year of cremation is approximatelyattacking healthy cells. The US now has "GLEEVAC"
50%. Offering storage and or profiling DNA of thewith identical results. It also has been proven that in
deceased, gives Funeral Directors a Uniquebreast cancers there are genetically divergent
opportunity to offer a Service that can have a lastingCLONES that account for different microscopic
impact on those we serve. If you as a Funeralcomponents resulting in different responses to
Director do not see the need for this service, it doestherapy.
not mean that families do not need this service.Future Direction
Statistics tell us that families place a tremendousAs the human genome Project continues to uncover
amount of trust in their Funeral Director. This isimportant disease genes (especially those for
because we care so deeply in what we do. Informingcommon disorders) at an ever increasing rate and
a Family of their options, while guiding them throughtechnologies for high-speed DNA sequencing and
the most difficult times in their life is a responsibilitymultiplex mutation detection continued to improve,
that a Funeral Director accepts and excels in.we can anticipate diagnostic molecular genetics
It is our hope that Funeral Homes throughout theassuming a far more dominant role in public health and
United States will contact us and give us their inputpreventive medicine. The advance of DNA "CHIPS"
as to the value of DNA in a Funeral service.containing thousands of probes may someday allow
Why we firmly believe in what we do.extensive genotyping and lifetime disease prediction
At the National Funeral Directors Association meetingfor thousands of disorders from a single drop of
in October 2001, we outlined all the reasons for theblood. Also, a poster on Human Genome Landmarks
value of DNA storage such as paternity/inheritance,in the US Department of Energy, identifies a whole
genealogy, missing persons, forensic issues;gamut of diseases/disorders with the corresponding
identification of hereditary disorders, congenital birthposition of the defective gene! Against these
defects; predisposition to allergies, mental, metabolic,promising advances will have to be weighed ethical
cardiovascular, bleeding/clotting disorders, geneticissues, especially in the field of gene therapy.
cancers, microbial diseases. The potential does notWhatever the ultimate balance reached, there's no
end with the above. Rapidly evolving technologies indoubt that molecular genetics will be the driving force
cloning pets, stem cell/gene therapy are currentlybehind an ever greater proportion of evidence based
being done, all to improve the quality of life.medical practice in the 21st century and virtually
Recently we had four interesting success stories...every patient whether healthy or ill will feel the
1. A 62-year-old female dies of complications resultingimpact.
from Breast Cancer. The deceased women leave 2The impact of DNA storage on clinical practice
daughters and 1 granddaughter. During a "Pre-NeedEvidence based medicine is the gold standard for the
Consultation", the woman elected to have her DNA21st century.
profiled and the sample banked.What do we do that contributes to the practice of
2 years later; one of the daughters is diagnosed withthis medicine? What specific examples and daily living
the same Breast Cancer as the Mother. The secondindicate that storing DNA is a "Must"?
daughter has her DNA profiled and compared to theThe event of 9/11 mainly profiling and identifying the
mothers. It is determined that the second daughterdeceased was laborious and expensive on federal
does not have the same genetic structure as thefunds despite which only approximately 2000 persons
mother that would pre-dispose her to the cancer.have been identified. One does not realize the
However, the Granddaughters DNA is profiled and itimportance of the death certificate without which
is determined that she possesses the same geneticburial cannot be accomplished until death occurs!
disorder as the Grandmother. Pharmacogenomics andSoldiers "missing in action" cannot be declared dead
gene therapy are begun to prevent the cancer in theuntil their bodies are found and identified.
granddaughter before it develops.An article in USA Today concerned a "Mystery killer"
2. The mother of a Divorced son was interested inthat involved a young couple; studies failed to give a
identifying the granddaughter's father. Was he herdefinitive answer despite autopsy and numerous
husband were her son? We identified her son is thelaboratory tests. Since chances that the suspected
alleged father. This was a "Paternity" issue.disease that clinically presented to be contagious
3. The three sons of the deceased lady came to(plague) proved negative on repeated testing. Had
request identification of their mothers remainsDNA been stored, further testing may have led to
between two occupants of a gravesite that hadthe diagnosis and cause of death
collapsed. She passed away seven years ago, so theA TV program about a Serial killer in Juarez Mexico
atypical specimen sources were bone marrow andled to more than 200 missing women and "no leads".
vertebrae. Procedures were laborious, but weProfiling and storing of DNA when these women
identified their mother. Her remains can now bewere newborns would have helped identify the
transferred to another site. This is "Profiling".remains that took months to surface. The women
4. A friend's baby presented with what appeared toafter being raped were doused with gasoline and
be a Bleeding tendency at 3 months of age. Theburned! The problem is ongoing.
baby was admitted to Children's Hospital, Cincinnati,Although Chandra Levy was missing for a year
extensively treated but expired at age 8 months. Anbefore the body was found, DNA is stable, and after
autopsy revealed universal capillary involvement (smallprofiling samples from her remains she can now be
blood vessels) by a clotting abnormality resulting inlaid to rest. Since degraded DNA is difficult to purify,
damaging complications in vital organs such as heart,tests on her remains are ongoing to hopefully identify
liver and spleen. This leaves a Protein called vonthe killer. The FBI in USA Today declared, "there still
Willebrand factor and is coded by a Gene calledare no clues to the killer". Samples are from her
ADAMSTS 13. The parents are currently being testedremains such as hair, teeth, bone; even old blood can
for "Mutations" in order to know who transmitted tostill be stored and tested along with a Suspect's
the gene. The baby's DNA is currently in storage itsamples until results are conclusive.
doesn't matter who stores DNA in life and in deathA complex disease such as Parkinson's disease and
provided it is properly collected and stored becausethe genes whose polymorphic forms can increase
although it's stable, it can be contaminated and it canany person's risk but not necessarily cause it is the
disappear during purification; this complicates geneticsecond most common in a Neuron-degenerative
testing. Before the advent of Pharmacogenomics,disorder. Parkinson's disease has neither a Polygenic
astute clinicians treating HIV patients relied on drug(multiple genes) or multifactoral (genes and
resistance testing to predict outcomes;environment) cause. Over the past few years,
complementary to resistance testing his currentdebate has occurred between Parkinson's disease
genotyping, which includes identifying mutations,having a Genetic component or is just secondary to
associated with resistance. In the not-too-distantenvironmental influences. To evaluate the possible
future, the combination of drug resistance testinggenetic component, open quote gene mapping" is the
and pharmacokinetic testing will provide a better ideaway to go. The availability of data from the Human
of in-vivo relevance of resistance data. Stored DNAGenome Project is opening new possibilities in
lasts forever; it will provide an endless source forstudying common diseases such as Parkinson's
multiple testing that will hopefully improve clinicaldisease. The multitude of molecular techniques and
outcomes.statistical tools applied to this data now allows us to
Pharmacogenomicspotentially move medicine from a "reactive" discipline
The terms "Pharmacogenomics" andto one that can prevent disease. However, once
"Pharmacokinetics" are sometimes usedfound, how these "susceptibility genes" will be used in
interchangeably to describe the analysis of genesthe future remains to be seen.
involved in drug response.A newborn (the 3rd child) was diagnosed to have a
Pharmacogenomics is more inclusive; it refers not only"Rare protein allergy". Surgery was successful the
to the effects of individual genes, but also tobaby is now seven years of age and healthy. Two
complex interaction between genes from every partother siblings are healthy. Storing this baby's DNA
of the genome affecting drug response.would have enabled testing of future siblings for
Pharmacogenomics is an aid to diagnosis andmutations related to this rare congenital predisposition
prognosis. Routine diagnosis is not alwaysto allergies.
straightforward. A patient does not always comeAt three months of age a Baby presented with a
with textbook type symptoms of the disease. InBleeding disorder; she was admitted, traded and died
some cases, a single gene variation has been shownat the Children's Hospital in Cincinnati. The baby's
to be responsible for disease, and a Genetic test forprofile showed a defective ADAMSTS 13 gene. The
this scan confirms the diagnosis as in cystic fibrosisparents are being tested for this "mutation" and the
and Huntington's disease. Sometimes more than onebaby's blood, buccal smears, and hairs are stored.
gene is involved, such as to Breast Cancer genes,Will everyone be gene type early in life to prevent
Alzheimer's Disease genes, and susceptibility todisease that they are at risk for? How will this affect
Migraine genes. The most likely publicly visibleemployment/applications for competitive educational
contribution of Pharmacogenomics to improved healthopportunities? Wolf farm code genetic genotyping be
care would be delivery of a number of drugs coupledroutine to determine patients with the risk for side
to diagnostic tests based on genetic markers foreffects or variability in efficacy? If the patient
head and neck, pancreatic cancers, and solid tumors.refuses typing will third-party payers is still pay for
Pharmacogenomics classifies patients into respondersmedications and/or treatment? Someday mandatory
and non-responders to particular therapeutic options.DNA storage and testing in life and death will enhance
Breast cancers that over express a Protein for thethe quality of life and improve clinical outcomes
herceptin genes are candidates for monoclonalbecause increasing knowledge of genetic variations
antibody therapy. The cholesterol-lowering drugsheds light on the role of genetic and environmental
PRAVACHOL works according to the number offactors and disease susceptibility, aggression and
copies of the transfer protein gene. HIV Phenotypingtherapeutic response.
is an important and practical adjunct to the treatmentSpecialists can now screen eggs for the faulty gene
of AIDS.that closes early onset Alzheimer's disease, enabling
Pharmacogenomics can save lives lost to adversewomen who carry their rare disorder to avoid
drug events, the 6th leading cause of death in thepassing it on to their children.
US. A blood test now enables physicians to tailor aFDA approved GLEEVEC has been very effective in
certain drug dosage to their patient's genetic profiles.chronic myelogenous leukemia and rare (stromal)
However, the cause and effect association remainsstomach cancers; causes of relapse do so because
unknown. Implementation of rapid automated DNAthey have developed mutations that alter GLEEVEC's
genotyping capabilities still, over time, providestarget site in the leukemic cells, a Phenomenon well
individual genotypes of patients. Clinical data that isknown to infectious disease clinicians. Just as
properly collected and managed identifies patientmicrobes developing drug resistance mutations, so do
subpopulations at risk for adverse events, whilecancer cells.
allowing others to continue to receive the benefits ofSummarizing the future of cancer treatment: in the
pharmaceutical therapy.past, pathologic diagnosis was based on histology. In
Pharmacogenomics and Gene Therapythe future it will be based on molecular profiling of
Mutation is a change of DNA sequence leading totissue both that the genetic and proteinomic level. In
aberrant or absent expression of the correspondingthe past, therapy was chosen by disease category.
protein. It is the mutation, not the gene that causesIn the future, combination therapy will be aimed in
predisposition to disorder/disease. Polymorphism istailored to individual patient profiles or classes of
the quality of existing in several different forms.profiles. Select, monitor, and reevaluate.. that's hope
Sequencing of parts of the genome hasfor the future!